Rare diseases can severely affect quality of life and life expectancy. Lysosomal storage disorders, such as #Fabry, #Gaucher, #Hunter, and #Sanfilippo diseases are a group of #rarediseases that currently lack a totally effective treatment.
Today, our Director of Business Development Alba Córdoba, will participate in the Nano Rare Diseases Day online event organized by NanomedSpain, talking about DELOS nanoliposomes for the treatment of Fabry disease during smart4fabry and PHOENIX OITB European projects.
Nanomol Technologies brings #know-how regarding nanoformulation of biological drug substances using the proprietary DELOS technology. We ensured adequate quantity and quality of drug product batches for #preclinical studies and also implemented #QualitybyDesign as a tool for robust manufacturing of enzyme loaded nanovesicles. Currently, we are working in the #GMP implementation of the #scaled-up process to enable the clinical testing of DELOS nanoliposomes for the treatment of Fabry disease.